Prion Disease Treatment: Milestones in Gene Editing Therapy

April 7, 2025

Prion disease treatment has taken a promising turn with groundbreaking research at Harvard, offering a glimmer of hope for those afflicted by these rare, fatal conditions caused by misfolded proteins.Among the most well-known forms of prion disease are Creutzfeldt-Jakob disease and fatal familial insomnia, each characterized by devastating neurological decline.
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